A framework for individualized splice-switching oligonucleotide therapy
Authors: Jinkuk Kim; Sijae Woo; Claudio M de Gusmao; Boxun Zhao; Diana H Chin; Renata L DiDonato; Minh A Nguyen; Tojo Nakayama; Chunguang April Hu; Aubrie Soucy; Ashley Kuniholm; Jennifer Karlin Thornton; Olivia Riccardi; Danielle A Friedman; Christelle Moufawad El Achkar; Zane Dash; Laura Cornelissen; Carolina Donado; Kamli N W Faour; Lynn W Bush; Victoria Suslovitch; Claudia Lentucci; Peter J Park; Eunjung Alice Lee; Al Patterson; Anthony A Philippakis; Brad Margus; Charles B Berde; Timothy W Yu
Collaborators: Ataxia Telangiectasia Children's Project; Boston Children's Hospital; Broad Institute of MIT and Harvard; Harvard Medical School; Korea Advanced Institute of Science and Technology; University of Campinas