A framework for individualized splice-switching oligonucleotide therapy

Jinkuk Kim, Sijae Woo, Claudio M de Gusmao, Boxun Zhao, Diana H Chin, Renata L DiDonato, Minh A Nguyen, Tojo Nakayama, Chunguang April Hu, Aubrie Soucy, Ashley Kuniholm, Jennifer Karlin Thornton, Olivia Riccardi, Danielle A Friedman, Christelle Moufawad El Achkar, Zane Dash, Laura Cornelissen, Carolina Donado, Kamli N W Faour, Lynn W Bush, Victoria Suslovitch, Claudia Lentucci, Peter J Park, Eunjung Alice Lee, Al Patterson, Anthony A Philippakis, Brad Margus, Charles B Berde, Timothy W Yu