A framework for individualized splice-switching oligonucleotide therapy

Al Patterson, Anthony A Philippakis, Ashley Kuniholm, Aubrie Soucy, Boxun Zhao, Brad Margus, Carolina Donado, Charles B Berde, Christelle Moufawad El Achkar, Chunguang April Hu, Claudia Lentucci, Claudio M de Gusmao, Danielle A Friedman, Diana H Chin, Eunjung Alice Lee, Jennifer Karlin Thornton, Jinkuk Kim, Kamli N W Faour, Laura Cornelissen, Lynn W Bush, Minh A Nguyen, Olivia Riccardi, Peter J Park, Renata L DiDonato, Sijae Woo, Timothy W Yu, Tojo Nakayama, Victoria Suslovitch, Zane Dash