Clinically important endpoints in individuals with leukodystrophy: A multisite study

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Date: November 11, 2025
Authors:
Adeline Vanderver, Ali Fatemi, Amanda Nagy, Amena Smith Fine, Amina Khan, Amy Pizzino, Amy Waldman, Ashley Hackett, Dandre Amos, Emma R Kotes, Florian Eichler, Francesco Gavazzi, Jacob McCann, Jamie Fraser, Jeilo Gauna, Johanna Schmidt, Jordan Goodman, Joshua Bonkowsky, Justine Shults, Kayla Muirhead, Keith Van Haren, Laura Adang, Lisa Emrick, Mariko Bennett, Mark Ramos, Nicole Page, Omar Sherbini, Robert Grundmeier, Russell D’Aiello, Sarah Woidill, Seungil Lee, Stephanie Keller
Journal: Annals of The Child Neurology Society