Paired-like homeobox gene (PHOX2B) nonpolyalanine repeat expansion mutations (NPARMs): genotype-phenotype correlation in congenital central hypoventilation syndrome (CCHS)

  • Authors: Amy Zhou; Casey M Rand; Sara M Hockney; Grace Niewijk; Patrick Reineke; Virginia Speare; Elizabeth M Berry-Kravis; Lili Zhou; Lawrence J Jennings; Min Yu; Isabella Ceccherini; Tiziana Bachett; Melanie Pennock; Kai Lee Yap; Debra E Weese-Mayer
  • Collaborators: Dip. Scienze della Terra dell'Ambiente e della Vita; IRCCS Istituto Giannina Gaslini; North Bristol NHS Trust; Northwestern University Feinberg School of Medicine; Rush University Medical Center; Stanley Manne Children's Research Institute, affiliated with Ann & Robert H. Lurie Children's Hospital of Chicago
  • Journal: Genetics in Medicine
  • Date: 2021 - Sep

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